gene therapy

Editing DNA could be genetic medicine breakthrough with ethical concerns
Images of normal (above) and diseased retinas. Patients with MFRP mutations, a cause of retinitis pigmentosa, lose the function of most retinal cells, particularly at the periphery of the retina, leaving them with drastically reduced vision. Personalized gene therapy, using iPS cells, may offer a way to correct this genetic disorder.
Patient-Specific Stem Cells and Personalized Gene Therapy
This shows regenerated auditory nerves after gene therapy (top) compared with no treatment (below). Credit: UNSW Translational Neuroscience Facility
Hearing quality restored with bionic ear technology used for gene therapy
An artistic rendering of human stem cells on the polymer scaffolds. Photo courtesy of Charles Gersbach and Farshid Guilak, Duke University
Gene Therapy Might Grow Replacement Tissue Inside the Body
Fixing a body’s broken genes is becoming possible
OHSU AIDS vaccine candidate appears to completely clear virus from the body
New Drug Improves Walking Performance for Duchenne Muscular Dystrophy Patients
Inhalable Gene Therapy May Help Pulmonary Arterial Hypertension Patients
New gene delivery method: magnetic nanoparticles
New Gene Therapy Shows Broad Protection in Animal Models to Pandemic Flu Strains, including the Deadly 1918 Spanish Influenza
Stem cell “homing” signal may help treat heart failure patients
UAB researchers cure type 1 diabetes in dogs
A way to use HIV to beat HIV
A Quantum Leap in Gene Therapy of Duchenne Muscular Dystrophy
Gene therapy reprograms scar tissue in damaged hearts into healthy heart muscle