In a small and preliminary clinical trial, Johns Hopkins researchers and their collaborators have shown that an experimental gene therapy that uses viruses to introduce a therapeutic gene in... Read more
For millions of sufferers, there is nothing more debilitating than chronic back or joint pain. It can feel like a lifetime of misery. But researchers led by University of Utah bioengi... Read more
In the summer of 2015, a team at Boston Children’s Hospital and Harvard Medical School reported restoring rudimentary hearing in genetically deaf mice using gene therapy. Now the Bost... Read more
Mechanisms underlying direct programming of stem cells could eventually lead to cell-replacement therapies A team of scientists has uncovered details of the cellular mechanisms that control... Read more
Eye diseases such as diabetic retinopathy and age-related macular degeneration are among the leading causes of irreversible vision loss and blindness worldwide. Currently, gene therapy can b... Read more
A discovery by Washington State University scientist Dan Rodgers and collaborator Paul Gregorevic could save millions of people suffering from muscle wasting disease. The result of the team’... Read more
Channel blocker drug, added to regenerative factors, is key Research from Boston Children’s Hospital suggests the possibility of restoring at least some visual function in people blinded by... Read more
Millions of adults over age 50 struggle each year with vision loss caused by damage to the retina or common macular degeneration. Physics researchers at The University of Texas at Arlington... Read more
Muscular dystrophy, which affects approximately 250,000 people in the U.S., occurs when damaged muscle tissue is replaced with fibrous, fatty or bony tissue and loses function. For years, sc... Read more
Team from Oxford and Stony Brook first to use optogenetics to control excitation waves in heart cells We depend on electrical waves to regulate the rhythm of our heartbeat. When those signal... Read more
Deep learning has already had a huge impact on computer vision and speech recognition, and it’s making inroads in areas as computer-unfriendly as cooking. Now a new startup led by Univ... Read more
Surprisingly rapid regrowth of unused brain connections after decades of near blindness Since 2007, clinical trials using gene therapy have resulted in often-dramatic sight restoration for d... Read more
How it lives in boiling acid offers template for delivering gene therapy By unlocking the secrets of a bizarre virus that survives in nearly boiling acid, scientists at the University of Vir... Read more
Researchers from the Salk Institute for Biological Studies in La Jolla, CA, report success for the first time in using gene-editing technology to prevent multiple human mitochondrial disease... Read more
Bioengineers at The University of Texas at Dallas have created a novel gene-delivery system that shuttles a gene into a cell, but only for a temporary stay, providing a potential new gene-th... Read more